TABLE 1 Clinical Trial Phases Applicable to Microbicides
Phase Number of Participants Length of Treatment and Follow-up Objectives
Phase I 10–100 1 to 2 weeks To assess local and systemic safety and acceptability and to determine dose and formulation. May run into a phase II trial (called phase I/II).
Phase II 50–200 2 to 6 months To assess safety and acceptability over a longer time.
Phase II/IIb 50–500 6 months to 2 years To screen for products reaching a minimum level of effectiveness. Smaller, less costly than phase III, but numbers of participants and length of follow-up indicate whether a subsequent larger trial would be worthwhile. If so, participants continue from one trial to the next, and additional participants are recruited (called phase II/III).
Phase III 1,000–30,000 1 to 2 years To evaluate effectiveness in preventing HIV infection and other STIs and to assess long-term safety and acceptability. Some phase III trials will involve multiple products, which will require more participants than those testing only one product.

Note: Phases I/II, II/IIb, and II/III are variants of study designs or studies that move from one clinical trial phase to the next. Number of participants and length of treatment and follow-up vary. Sources: Adapted from Stone, 2003 (112), Fleming, 2004 (27), Mauck et al., 2001 (71), and the Alliance for Microbicide Development, 2004 (3).

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